Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy | MicrobiomeTrials← Back to trialsNCT05933057
Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy
RecruitingPHASE3INTERVENTIONAL
Trial Details
Start: 2024-02-19Est. Completion: 2028-02
Enrollment target: 138 participants Locations- Universitaire Ziekenhuizen Leuven, Leuven, Belgium
- British Columbia Children's Hospital, Vancouver, British Columbia, Canada
- The University of Western Ontario - Children's Health Research Institute, London, Ontario, Canada
- University of Ottawa - Children's Hospital of Eastern Ontario, Ottawa, Ontario, Canada
- University of Toronto - Holland Bloorview Kids Rehabilitation Hospital, Toronto, Ontario, Canada
- Klinika dětské neurologie 2. LF, Fakultní nemocnice v Motole, Prague, Czechia
- Centre Hospitalier Régional Universitaire de Lille, Lille, France
- Centre hospitalier universitaire - Hôpitaux de Marseille, Marseille, France
- Hôpital Armand-Trousseau - I-Motion, Paris, France
- Charite-Universitaetsmedizin Berlin, Berlin, Germany
- Universitätsklinikum Essen Kinder-und Jugendmedizin Neuropadiatrie, Essen, Germany
- Universitaetsklinikum Freiburg, Freiburg im Breisgau, Germany
- Universitätsklinikum Hamburg-Eppendorf, Klinik und Poliklinik für Kinder- und Jugendmedizin, Hamburg, Germany
- Associazione La Nostra Famiglia - IRCCS Eugenio Medea - Bosisio Parini, Lecco, Italy
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Fondazione Serena Onlus - Azienda Ospedaliera Niguarda Ca' Granda - NeuroMuscular Omnicentre, Milan, ItalyUniversità degli Studi di Padova - Azienda Ospedaliera di Padova, Padova, ItalyOspedale Pediatrico Bambino Gesù, Roma, ItalyPoliclinico Universitario Agostino Gemelli - Università Cattolica del Sacro Cuore, Roma, ItalyLeids Universitair Medisch Centrum (LUMC), Leiden, NetherlandsRadboud Universitair Medisch Centrum (Radboudumc), Nijmegen, NetherlandsUniwersyteckie Centrum Kliniczne, Klinika Neurologii Rozwojowej, Gdansk, PolandUniwersyteckie Centrum Kliniczne WUM, Centralny Szpital Kliniczny, Warsaw, PolandClinic of Neurology and Psychiatry for Children and Youth, Belgrade, SerbiaHospital Sant Joan de Déu, Barcelona, SpainHospital Universitario y Politécnico La Fe, Valencia, SpainKarolinska University Hospital, Solna CKB Centrum för Kliniska Barnstudier, Stockholm, SwedenNewcastle upon Tyne Hospitals NHS Foundation Trust - Newcastle University, Newcastle upon Tyne, England, United KingdomOxford University Hospitals NHS Foundation Trust, Oxford, England, United KingdomNHS Greater Glasgow and Clyde - Royal Hospital for Children, Glasgow, Scotland, United Kingdom