A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1) | MicrobiomeTrials← Back to trialsNCT06185764
A Phase 1/2 Study of VX-670 in Adult Participants With Myotonic Dystrophy 1 (DM1)
RecruitingPHASE1, PHASE2INTERVENTIONAL
Trial Details
Start: 2024-02-20Est. Completion: 2027-02-02
Enrollment target: 52 participants Locations- Stanford Neuromuscular Research, San Carlos, California, United States
- University of Florida Clinical Research Center, Gainesville, Florida, United States
- University of Kansas Medical Center, Fairway, Kansas, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Washington University School of Medicine / St. Louis Children's Hospital, St Louis, Missouri, United States
- Wake Forest Baptist Health, Winston-Salem, North Carolina, United States
- University of Pennsylvania, Philadelphia, Pennsylvania, United States
- Virginia Commonwealth University (Sanger Hall), Richmond, Virginia, United States
- Wesley Research Institute, Auchenflower, Australia
- Neuroscience Clinical Trials Unit, Alfred Brain, Melbourne, Australia
- Universitaire Ziekenhuizen Leuven - Campus Gasthuisberg, Leuven, Belgium
- Hopital de Chicoutimi, Chicoutimi, Canada
- Altasciences Montreal, Montreal, Canada
- McGIll University, Montreal, Canada
- University of Ottawa, Ottawa, Canada
- CHU Research Centre of Quebec, Québec, Canada
- Neuromuscular Reference Center Institute of Myology, Paris, France
- Ludwig Maximilians Universitaet Muenchen, München, Germany
- Centro Clinico NeMO, Milan, Italy
- Maastricht University Medical Center, Maastricht, Netherlands
- Hospital Universitario y Politécnico La Fe, Valencia, Spain
- Clinical Research Facility, Queen Elizabeth University Hospital, Glasgow, United Kingdom
- Leonard Wolfson Experimental Neurology Centre CRF, London, United Kingdom
- St. George's University Hospital, London, United Kingdom
- Salford Royal Hospital, Salford, United Kingdom
- Royal Hallamshire Hospital, Sheffield, United Kingdom
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