This site is for informational purposes only and does not provide medical advice, diagnosis, or treatment. Always consult your healthcare provider.
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy | MicrobiomeTrials
← Back to trials NCT06270719
An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy ENROLLING_BY_INVITATION OBSERVATIONAL
Read the full scientific description See full eligibility requirements Trial Details Start: 2024-02-07Est. Completion: 2028-12-31
Enrollment target: 500 participantsLocations Children's of Alabama, Birmingham, Alabama, United States Arkansas Children's Hospital, Little Rock, Arkansas, United States Children's Hospital Los Angeles, Los Angeles, California, United States University of Colorado - PPDS, Aurora, Colorado, United States Connecticut Children's Medical Center - Hartford, Hartford, Connecticut, United States Children's National, Washington D.C., District of Columbia, United States Nicklaus Children's Hospital, Miami, Florida, United States Nemours Children's Hospital - Orlando, Orlando, Florida, United States All Children's Research Institute, Inc, St. Petersburg, Florida, United States Ann and Robert H Lurie Childrens Hospital of Chicago, Chicago, Illinois, United States Indiana Clinical and Translational Science Institute, Indianapolis, Indiana, United States University of Kansas Medical Center, Kansas City, Kansas, United States Norton Children's Neuroscience Institute - Louisville, Louisville, Kentucky, United States Boston Children's Hospital, Boston, Massachusetts, United States University of Michigan, Ann Arbor, Michigan, United States Other microbiome trials you might be interested in Spinal Amyotrophy
Spinal muscular atrophy (SMA) is a rare neuromuscular disease causing progressive muscle weakness related to degeneratio…
Liège, Belgium Est. completion Mar 28, 2028
Duchenne Muscular Dystrophy (DMD) Chronic Pain Neuromuscular Diseases (NMD)
1\. Brief Summary This prospective observational study aims to evaluate the 6-month longitudinal changes in chronic pain…
Antalya, Turkey (Türkiye) Est. completion Nov 30, 2026
UNM Clinical and Translational Science Center, Albuquerque, New Mexico, United States
Stony Brook Medicine Advanced Specialty Care, Stony Brook, New York, United States
Duke Lenox Baker Children's Hospital, Durham, North Carolina, United States
Childrens Hospital Medical Center of Akron, Akron, Ohio, United States
OHSU Healthcare (Oregon Health and Science University), Portland, Oregon, United States
Penn State Health Milton S. Hershey Medical Center, Hershey, Pennsylvania, United States
Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
Vanderbilt University Medical Center, Nashville, Tennessee, United States
Cook Children's Hospital, Fort Worth, Texas, United States
University of Virginia, Charlottesville, Virginia, United States
Children's Hospital of the King's Daughters, Norfolk, Virginia, United States
Seattle Children's Hospital, Seattle, Washington, United States
The Board of Regents of the University of Wisconsin, Madison, Wisconsin, United States
The Medical College of Wisconsin, Milwaukee, Wisconsin, United States