Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous Disease | MicrobiomeTrials← Back to trialsNCT06325709
Base Editing for Mutation Repair in Hematopoietic Stem & Progenitor Cells for X-Linked Chronic Granulomatous Disease
RecruitingPHASE1, PHASE2INTERVENTIONAL
Trial Details
Start: 2024-04-17Est. Completion: 2032-12-31
Enrollment target: 10 participants Locations- National Institutes of Health Clinical Center, Bethesda, Maryland, United States
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