Long-term Extension of GTX-102 in Angelman Syndrome | MicrobiomeTrials← Back to trialsNCT06415344
Long-term Extension of GTX-102 in Angelman Syndrome
ENROLLING_BY_INVITATIONPHASE3INTERVENTIONAL
Trial Details
Start: 2024-07-31Est. Completion: 2029-02
Enrollment target: 255 participants Locations- University of California, Los Angeles (UCLA), Los Angeles, California, United States
- University of California, San Diego - Rady Children's Hospital, San Diego, California, United States
- Rare Disease Research, LLC, Atlanta, Georgia, United States
- Rush University Medical Center, Chicago, Illinois, United States
- Boston Children's Hospital, Boston, Massachusetts, United States
- Weill Cornell Medicine, New York, New York, United States
- Queensland Children's Hospital, South Brisbane, Queensland, Australia
- The Royal Children's Hospital, Melbourne, Victoria, Australia
- MAGIC Clinic Ltd, Calgary, Alberta, Canada
- British Columbia Children's Hospital, Vancouver, British Columbia, Canada
- Childrens Hospital London Health Sciences Centre, London, Ontario, Canada
- Childrens Hospital of Eastern Ontario, Ottawa, Ontario, Canada
- The Research Institute of the McGill University Health Centre, Montreal, Quebec, Canada
- AP-HM - Hopital de la Timone, Marseille, France
- AP-HP Hopital Necker-Enfants Malades, Paris, France
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