RB001 Gene Therapy Study in Children With SHANK3-related Phelan-McDermid Syndrome (PMS) | MicrobiomeTrials← Back to trialsNCT07014020
RB001 Gene Therapy Study in Children With SHANK3-related Phelan-McDermid Syndrome (PMS)
RecruitingPHASE1INTERVENTIONAL
Trial Details
Start: 2025-06-16Est. Completion: 2027-05-01
Enrollment target: 8 participants Locations- Peking University First Hospital, Beijing, Beijing Municipality, China
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