Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD) | MicrobiomeTrials← Back to trialsNCT07123155
Study of S-606001 as an Add-on to Enzyme Replacement Therapy (ERT) in Participants With Late-onset Pompe Disease (LOPD)
RecruitingPHASE2INTERVENTIONAL
Trial Details
Start: 2025-10-30Est. Completion: 2027-08-08
Enrollment target: 45 participants Locations- University of California - Irvine Medical Center, Irvine, California, United States
- University of Florida (UF) - Gainesville, Gainesville, Florida, United States
- Emory University Hospital, Atlanta, Georgia, United States
- Washington University in St. Louis, St Louis, Missouri, United States
- Duke University Medical Center, Durham, North Carolina, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- University of Pennsylvania, Philadelphia, Pennsylvania, United States
- University of Pittsburgh School of Medicine, Pittsburgh, Pennsylvania, United States
- Lysosomal and Rare Disorders Research and Treatment Center (LDRTC), Fairfax, Virginia, United States
- UZ Leuven, Leuven, Belgium
- Aarhus University Hospital, Aarhus, Denmark
- HLC Hopital Pierre Wertheimer, Bron, France
- AP-HP Hopital Raymond Poincare, Garches, France
- Centre de Reference des Maladies Neuromusculaires et de la SLA - AP-HM Hopital de La Timone, Marseille, France
- CHU de Nice - Hopital Pasteur 2 - Centre de reference des Maladies Neuromusculaires, Nice, France
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