Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia | MicrobiomeTrials← Back to trialsNCT07441876
Study to Evaluate the Efficacy and Safety of BMN 333 Versus Vosoritide in Children With Achondroplasia
RecruitingPHASE2, PHASE3INTERVENTIONAL
Trial Details
Start: 2026-04-20Est. Completion: 2029-06
Enrollment target: 160 participants Locations- UCSF Benioff Children's Hospital Oakland, Oakland, California, United States
- Nemours Children's Health, Wilmington, Delaware, United States
- Ann & Robert H. Lurie Children's Hospital of Chicago, Chicago, Illinois, United States
- Johns Hopkins Medicine, Baltimore, Maryland, United States
- Cincinnati Children's Hospital Medical Center, Cincinnati, Ohio, United States
- Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Texas Children's Hospital, Dallas, Texas, United States
- Texas Children Hospital, Baylor College of Medicine, Houston, Texas, United States
- Consano Clinical Research, LLC, San Antonio, Texas, United States
- Murdoch Children's Research Institute, Parkville, Victoria, Australia
- McGill University Health Centre, Québec, Monteral, Canada
- Universite de Montreal - Centre Hospitalier Universitaire Sainte-Justine, Montreal, Quebec, Canada
- Irccs Ospedale Gaslini Di Genova, Genova, Italy
- Fondazione IRCCS Ca Grande Ospedale Maggiore, Milan, Italy
- Hokkaido University Hospital, Hokkaido, Japan
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