NCT07685314

LATE-ONSET POMPE DISEASE AND CEREBROVASCULAR MANIFESTATIONS

CompletedOBSERVATIONAL

Trial Details

Start: 2020-05-01Est. Completion: 2025-04-16

Enrollment target: 477 participants

Locations

Pompe Disease (Late-onset)Pompe Disease Late-OnsetLOPD

This is a single-arm, open-label, dose-escalation study to evaluate the safety, tolerability and efficacy of a single in…

Phoenix, United StatesEst. completion Sep 2028

Pompe Disease (Late-onset)

Pompe disease is a genetic condition which causes muscle weakness over time. People with Pompe disease have a faulty gen…

Atlanta, United StatesEst. completion Jun 30, 2027

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