Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy | MicrobiomeTrials← Back to trialsNCT04281485
Study to Evaluate the Safety and Efficacy of PF-06939926 for the Treatment of Duchenne Muscular Dystrophy
RecruitingPHASE3INTERVENTIONAL
Trial Details
Start: 2020-11-05Est. Completion: 2024-05-15
Enrollment target: 114 participants Locations- Arkansas Children's Hospital, Little Rock, Arkansas, United States
- Arkansas Children's, Little Rock, Arkansas, United States
- UCLA Medical Center, Los Angeles, California, United States
- University of Florida, Gainesville, Florida, United States
- University of Iowa Hospitals and Clinics, Iowa City, Iowa, United States
- KU Clinical Research Center - Clinical and Translational Science Unit (CTSU) - Fairway, Fairway, Kansas, United States
- KU Clinical Research Center - Clinical and Translational Science Unit (CTSU) - Rainbow, Kansas City, Kansas, United States
- University of Kansas Hospital - Investigational Pharmacy, Kansas City, Kansas, United States
- University of Kansas Hospital - Pediatric and Pediatric ICU - Operating Room, Kansas City, Kansas, United States
- University of Kansas Medical Center, Kansas City, Kansas, United States
- Pediatric Cardiology, Prairie Village, Kansas, United States
- Lenox Baker Children's Hospital, Durham, North Carolina, United States
- The Children's Hospital of Philadelphia, Philadelphia, Pennsylvania, United States
- Primary Childrens Hospital, Salt Lake City, Utah, United States
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University of Utah Clinical Neurosciences Center, Salt Lake City, Utah, United StatesUniversity of Utah Hospital, Salt Lake City, Utah, United StatesSeattle Children's, Seattle, Washington, United StatesThe Children's Hospital at Westmead, Westmead, New South Wales, AustraliaThe Royal Children's Hospital Melbourne, Parkville, Victoria, AustraliaPerth Children's Hospital, Nedlands, Western Australia, AustraliaUZ Gent, Ghent, BelgiumUZ leuven, Leuven, BelgiumAlberta Children's Hospital, Calgary, Alberta, CanadaChildren's Hospital - London Health Sciences Centre, London, Ontario, CanadaChildrens Hospital of Eastern Ontario, Ottawa, Ontario, CanadaThe Hospital For Sick Children, Toronto, Ontario, CanadaCHU de Nantes- Hotel Dieu, Nantes, FranceHopital Necker, Paris, FranceCharité - Universitätsmedizin Berlin, Berlin, GermanyUniversitatsklinikum Essen, Essen, GermanyHadassah University Medical Center, Ein Kerem, Jerusalem, IsraelSchneider Children's Medical Center of Israel, Petach Tikvah, IsraelFondazione Policlinico Universitario Agostino Gemelli IRCCS, Roma, ItalyIRCCS Ospedale Pediatrico Bambino Gesù, Rome, ItalyNagoya City University Hospital, Nagoya, Aichi-ken, JapanHyogo College of Medicine College Hospital, Nishinomiya, Hyōgo, JapanNational Center of Neurology and Psychiatry, Tokyo, JapanSaint Petersburg State Paediatric Medical University, Saint Petersburg, RussiaState Autonomous Healthcare Institution of Sverdlovsk Region Children's City Clinical Hospital No 9, Yekaterinburg, RussiaPusan National University Yangsan Hospital, Yangsan, Gyeongsangnam-do, South KoreaSeoul National University Hospital, Seoul, South KoreaSamsung Medical Center, Seoul, South KoreaHospital Sant Joan de Déu, Esplugues de Llobregat, Barcelona, SpainHospital Universitario Vall d'Hebron, Barcelona, SpainHospital Universitari i Politecnic La Fe de Valencia, Valencia, SpainInselspital, University Children's Hospital Berne, Bern, SwitzerlandUniversitaets-Kinderspital Zuerich, Zurich, SwitzerlandKaohsiung Medical University Chung-Ho Memorial Hospital, Kaohsiung City, TaiwanNational Taiwan University Hospital, Taipei, TaiwanTaipei Veterans General Hospital, Taipei, TaiwanThe Newcastle upon Tyne Hospitals NHS Foundation Trust, Royal Victoria Infirmary, Newcastle upon Tyne, England, United KingdomAlder Hey Children's NHS Foundation Trust, Liverpool, Merseyside, United KingdomGreat Ormond Street Institute of Child Health, London, United KingdomPhase 2
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